Mutation-specific cystic fibrosis treatments on verge of approval

Nat Med. 2011 Apr;17(4):396-7. doi: 10.1038/nm0411-396.
No abstract available

Publication types

  • News

MeSH terms

  • Aminophenols / therapeutic use
  • Cystic Fibrosis / drug therapy*
  • Cystic Fibrosis / genetics*
  • Cystic Fibrosis Transmembrane Conductance Regulator / agonists
  • Cystic Fibrosis Transmembrane Conductance Regulator / chemistry
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Drug Approval
  • Drug Discovery
  • Humans
  • Models, Molecular
  • Mutant Proteins / agonists
  • Mutant Proteins / chemistry
  • Mutant Proteins / genetics
  • Mutation
  • Quinolones / therapeutic use

Substances

  • Aminophenols
  • CFTR protein, human
  • Mutant Proteins
  • Quinolones
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • ivacaftor